Indication
Pyruvate Dehydrogenase Complex Deficiency
2 clinical trials
3 products
Clinical trial
Phase 3 Trial of Dichloroacetate in Pyruvate Dehydrogenase Complex Deficiency:Status: Active (not recruiting), Estimated PCD: 2025-03-30
Product
DichloroacetateProduct
GenotypeClinical trial
An Open Label, Exploratory, Proof-of Concept Study of Triheptanoin as Treatment for Patients With Primary-Specific Pyruvate Dehydrogenase Complex (PDC) DeficiencyStatus: Recruiting, Estimated PCD: 2026-12-31
Product
Triheptanoin