Indication
Severe Combined Immunodeficiency (SCID)
2 clinical trials
2 products
Clinical trial
An Observational Long-term Follow-up Study for Patients Previously Treated With Autologous ex Vivo Gene Therapy for Severe Combined Immunodeficiency Due to Adenosine Deaminase Deficiency (ADA-SCID)Status: , Estimated PCD: 2035-08-01
Product
EFS-ADA LVClinical trial
Bilateral Orthotopic Lung Transplant in Tandem With CD3+ and CD19+ Cell Depleted Bone Marrow Transplant From Partially HLA-Matched Cadaveric DonorsStatus: , Estimated PCD: 2025-11-01