Indication

Transfusion-dependent Alpha-Thalassemia

1 clinical trial

1 product

Clinical trial

A Phase 1 Open Label Study Evaluating the Safety and Efficacy of Gene Therapy in Subjects With Transfusion-dependent α-Thalassemia by Transplantation of Autologous CD34+ Cells Transduced Ex Vivo With a Lentiviral Vector (GMCN-508A Drug Product)

Status: Recruiting, Estimated PCD: 2028-08-01

Product