Indication
Amyloid Neuropathies
3 clinical trials
3 products
Clinical trial
APOLLO: A Phase 3 Multicenter, Multinational, Randomized, Double-blind, Placebo-controlled Study to Evaluate the Efficacy and Safety of Patisiran (ALN-TTR02) in Transthyretin (TTR)-Mediated Polyneuropathy (Familial Amyloidotic Polyneuropathy-FAP)Status: Completed, Estimated PCD: 2017-08-01
Product
PatisiranProduct
Sterile Normal SalineClinical trial
Expanded Access Protocol of Patisiran for Patients With Hereditary Transthyretin-Mediated Amyloidosis (hATTR Amyloidosis) With PolyneuropathyStatus:
Clinical trial
Evaluation of a New Diagnostic Approach to Familial Amyloid Neuropathy by Mutation of the TTR Gene in a Population of Idiopathic Chronic NeuropathiesStatus: Completed, Estimated PCD: 2020-05-27
Product
TTR