Indication
Late-Infantile Neuronal Ceroid Lipofuscinosis Type 2
2 clinical trials
3 products
Product
Cerliponase AlfaClinical trial
Cerliponase Alfa Observational StudyStatus: Active (not recruiting), Estimated PCD: 2030-08-31
Product
CerliponaseProduct
BMN190Clinical trial
A Phase 2, Open-Label, Multicenter Study to Evaluate Safety, Tolerability, and Efficacy of Intracerebroventricular BMN 190 in Pediatric Patients < 18 Years of Age With CLN2 DiseaseStatus: Completed, Estimated PCD: 2022-04-20