Indication
Congenital Myasthenic Syndrome
2 clinical trials
2 products
Product
AmifampridineClinical trial
A Phase 1b, Double-Blinded, Randomized, Placebo-Controlled Study to Assess the Safety, Tolerability, Pharmacokinetics, Immunogenicity, and Efficacy of ARGX-119 in Adult Participants With DOK7-Congenital Myasthenic SyndromesStatus: Not yet recruiting, Estimated PCD: 2025-10-01
Product
ARGX-119