Indication
Adenosine Deaminase Deficiency
1 clinical trial
1 product
Clinical trial
An Observational Long-term Follow-up Study for Patients Previously Treated With Autologous ex Vivo Gene Therapy for Severe Combined Immunodeficiency Due to Adenosine Deaminase Deficiency (ADA-SCID)Status: , Estimated PCD: 2035-08-01
Product
EFS-ADA LV