Indication
Jansky-Bielschowsky Disease
1 clinical trial
1 product
Product
BMN190Clinical trial
A Phase 2, Open-Label, Multicenter Study to Evaluate Safety, Tolerability, and Efficacy of Intracerebroventricular BMN 190 in Pediatric Patients < 18 Years of Age With CLN2 DiseaseStatus: Completed, Estimated PCD: 2022-04-20