Indication
Inherited Bone Marrow Failure Syndrome
3 clinical trials
3 products
2 drugs
Clinical trial
A Study Evaluating BPX-501 T Cells and AP1903 for Prevention of Graft Versus Host Disease (GVHD) After Haploidentical, Related, T Cell-Depleted Hematopoietic Cell Transplantation for Non-Malignant DiseasesStatus: Terminated, Estimated PCD: 2015-09-01
Product
BPX-501Product
BPX-501 and RimiducidClinical trial
Phase Ib Study of Imatinib to Increase RUNX1 Activity in Participants With Germline RUNX1 DeficiencyStatus: Recruiting, Estimated PCD: 2026-10-30
Drug
imatinibClinical trial
A Pilot Study to Evaluate the Feasibility of Post-Hematopoietic Stem Cell Transplant Prophylaxis With Decitabine Combined With Filgrastim for Children and Young Adults With AML, MDS and Related Myeloid MalignanciesStatus: Recruiting, Estimated PCD: 2026-09-01
Product
DecitabineDrug
Filgrastim