Indication
Glycogen Storage Disease Type 1A
1 clinical trial
3 products
Clinical trial
A Phase 3, Randomized, Double-Blind, Placebo-Controlled Study of Adeno-Associated Virus Serotype 8-Mediated Gene Transfer of Glucose-6-Phosphatase in Patients With Glycogen Storage Disease Type IaStatus: Active (not recruiting), Estimated PCD: 2024-02-20
Product
PlaceboProduct
Oral corticosteroidsProduct
DTX401