Indication

Mucopolysaccharidosis type 1

1 clinical trial

1 product

Clinical trial

A Phase 1/2 Open-Label, Sequential Dose-Escalation, Safety, Tolerability and Efficacy Study of SIG-005 in Adult Patients With Mucopolysaccharidoses 1 (MPS-1)

Status: Withdrawn, Estimated PCD: 2022-12-13

Product