Indication
Mucopolysaccharidosis Type I (MPS I)
1 clinical trial
1 product
Product
RGX-111Clinical trial
A Phase I/II Multicenter, Open-Label Study to Evaluate the Safety, Tolerability, and Pharmacodynamics of Intracisternal RGX-111 in Subjects With Mucopolysaccharidosis Type IStatus: Active (not recruiting), Estimated PCD: 2023-03-01