Indication
Pompe's Disease
3 clinical trials
3 products
Product
Alglucosidase alfaClinical trial
A Single Arm, Prospective, Open-label, Multi-center Study to Evaluate Efficacy and Safety in Chinese Patients With Late Onset Pompe Disease With Alglucosidase Alfa TreatmentStatus: Active (not recruiting), Estimated PCD: 2024-07-25
Product
Alglucosidase AlfaClinical trial
A Phase 3 Randomized, Multicenter, Multinational, Double-blinded Study Comparing the Efficacy and Safety of Repeated Biweekly Infusions of Avalglucosidase Alfa (neoGAA, GZ402666) and Alglucosidase Alfa in Treatment naïve Patients With Late-onset Pompe DiseaseStatus: Completed, Estimated PCD: 2020-03-19
Product
Avalglucosidase alfaClinical trial
An Open-label Ascending Dose Cohort Study to Assess the Safety, Pharmacokinetics, and Preliminary Efficacy of Avalglucosidase Alfa (NeoGAA, GZ402666) in Patients With Infantile-onset Pompe Disease Treated With Alglucosidase Alfa Who Demonstrate Clinical Decline or Sub-optimal Clinical ResponseStatus: Active (not recruiting), Estimated PCD: 2019-09-30