Indication
Exon 44
2 clinical trials
1 product
1 drug
Product
AOC 1044Clinical trial
A Phase 2 Open-label Study to Evaluate the Pharmacodynamics and Long-Term Safety and Tolerability of AOC 1044 Administered Intravenously to DMD Participants With Mutations Amenable to Exon 44 SkippingStatus: , Estimated PCD: 2025-12-31
Clinical trial
A Phase 1/2, Randomized, Placebo-controlled, Double-blind, Study to Evaluate the Safety, Tolerability, Pharmacokinetics, and Pharmacodynamic Effects of Single and Multiple Ascending Doses of AOC 1044 Administered Intravenously to Healthy Adult Volunteers and Participants With DMD Mutations Amenable to Exon 44 SkippingStatus: Recruiting, Estimated PCD: 2025-03-01
Drug
Varlilumab