Indication
autosomal recessive
2 clinical trials
2 products
Clinical trial
Dietary Treatment of Glucose Transporter Type 1 Deficiency (G1D)Status: Active (not recruiting), Estimated PCD: 2024-09-30
Product
TriheptanoinClinical trial
A Phase I/II, Non-Randomized, Open-Label Study of pCCLCHIM-p47 (Lentiviral Vector Transduced CD34+ Cells) in Patients With p47 Autosomal Recessive Chronic Granulomatous Disease (AR-CGD)Status: , Estimated PCD: 2027-03-31