Indication
Mitochondrial Encephalomyopathy
3 clinical trials
3 products
1 drug
Clinical trial
A Phase IIb Open-label, Multi-centre, Extension Study to Explore the Long-term Safety and Efficacy of KH176 in Subjects With a Genetically Confirmed Mitochondrial DNA tRNALeu(UUR) m.3243A>G Mutation Who Have Completed the KHENERGYZE Study KH176-202.Status: Completed, Estimated PCD: 2023-06-01
Product
KH176Clinical trial
A Phase II, Monocenter, Single Arm Study To Assess The Safety and Efficacy Of Combination Deoxycytidine and Deoxythymidine For Mitochondrial Depletion DisordersStatus: Recruiting, Estimated PCD: 2025-12-31
Clinical trial
A Phase III, Randomised, Double-blind, Placebo-controlled, Parallel-group, Pivotal Trial to Assess the Efficacy and Safety of Sonlicromanol in Adult Subjects With a Genetically Confirmed Mitochondrial DNA tRNALeu(UUR) m.3243A>G VariantStatus: Not yet recruiting, Estimated PCD: 2027-07-02
Product
SonlicromanolDrug
Varlilumab