Organization
Applied Genetic Technologies
1 clinical trial
Clinical trial
A Multiple-Site, Phase 1/2, Safety and Efficacy Trial of a Recombinant Adeno-associated Virus Vector Expressing Retinoschisin (rAAV2tYF-CB-hRS1) in Patients With X-linked RetinoschisisStatus: Completed, Estimated PCD: 2019-04-01