Organization
CorrectSequence Therapeutics
3 clinical trials
Clinical trial
A Single-arm, Open-label Phase I Clinical Trial to Evaluate the Safety, Tolerability, Efficacy, Pharmacokinetics and Pharmacodynamic Profile of a Single Dose of CS-101 Injection in Subjects With β-thalassemia MajorStatus: Recruiting, Estimated PCD: 2025-05-01
Clinical trial
A Clinical Study Evaluating the Safety and Efficacy of In-vitro tBE Edited Autologous Hematopoietic Stem Progenitor Cells(CS-101) in Treating Subjects With β-thalassemiaStatus: Active (not recruiting), Estimated PCD: 2024-12-31
Clinical trial
A Clinical Study Evaluating the Safety and Efficacy of In-vitro tBE Edited Autologous Hematopoietic Stem Progenitor Cells(CS-101) in Treating Subjects With β-thalassemiaStatus: , Estimated PCD: 2025-12-31