Organization
IntraBio
4 clinical trials
Clinical trial
Effects of N-Acetyl-L-Leucine on GM2 Gangliosidosis (Tay-Sachs and Sandhoff Disease): A Multinational, Multicenter, Open-label, Rater-blinded Phase II StudyStatus: Completed, Estimated PCD: 2023-01-09
Clinical trial
Effects of N-Acetyl-L-Leucine on Niemann-Pick Disease Type C (NPC): A Phase III, Randomized, Placebo-controlled, Double-blind, Crossover StudyStatus: Active (not recruiting), Estimated PCD: 2023-06-12
Clinical trial
Effects of N-Acetyl-L-Leucine on Ataxia-Telangiectasia (A-T): A Multinational, Multicenter, Open-label, Rater-blinded Phase II StudyStatus: Recruiting, Estimated PCD: 2024-12-01
Clinical trial
Effects of N-Acetyl-L-Leucine on Niemann Pick Type C Disease: A Multinational, Multicenter, Open-label, Rater-blinded Phase II Study.Status: Completed, Estimated PCD: 2022-11-07