Organization
JCR Pharmaceuticals
11 clinical trials
Clinical trial
An Extension Study of JR-141 to Evaluate the Long-term Safety and Efficacy in Mucopolysaccharidosis Type II (Hunter Syndrome) SubjectsStatus: , Estimated PCD: 2028-02-28
Clinical trial
A Phase III Study of JR-141 in Patients With Mucopolysaccharidosis II (STARLIGHT)Status: Recruiting, Estimated PCD: 2026-01-31
Clinical trial
An Extension Study of JR-171-101 Study in Patients With Mucopolysaccharidosis Type IStatus: Active (not recruiting), Estimated PCD: 2025-04-30
Clinical trial
An Extension Study of JR-141 in Patients With Mucopolysaccharidosis Type IIStatus: Active (not recruiting), Estimated PCD: 2030-03-31
Clinical trial
An Extension Study of JR-141-BR21 in Patients With Mucopolysaccharidosis IIStatus: Active (not recruiting), Estimated PCD: 2024-03-31
Clinical trial
Phase I/II Study of JR-171 ㏌ Patients With Mucopolysaccharidosis Type IStatus: Completed, Estimated PCD: 2022-08-02
Clinical trial
A Phase I/II Study of JR-141 in Patients With Mucopolysaccharidosis Type IIStatus: Completed, Estimated PCD: 2017-10-04
Clinical trial
Phase II Study of JR-141 in Patients With Mucopolysaccharidosis IIStatus: Completed, Estimated PCD: 2019-10-04
Clinical trial
A Phase II/III Study of JR-141 in Patients With Mucopolysaccharidosis IIStatus: Completed, Estimated PCD: 2020-02-20
Clinical trial
Phase I/II Study of Weekly Infusions of JR-441 in Patients With Mucopolysaccharidosis Type IIIAStatus: Recruiting, Estimated PCD: 2029-10-31
Clinical trial
An Open-label Phase I/II Study of JR-446 in Mucopolysaccharidosis Type IIIBStatus: Not yet recruiting, Estimated PCD: 2027-03-31