Organization
Elixirgen Therapeutics
2 clinical trials
Clinical trial
A Phase I/II Study to Evaluate the Safety and Tolerability of EXG34217 in Patients With Telomere Biology Disorders With Bone Marrow FailureStatus: Recruiting, Estimated PCD: 2027-04-08
Clinical trial
Long Term Follow-up Study in Patients With Telomere Biology Disorders With Bone Marrow Failure Who Completed Study EXG-US-01Status: Not yet recruiting, Estimated PCD: 2027-01-30