Organization
Recordati Rare Diseases
4 clinical trials
Clinical trial
Understanding the Long-Term Management of Organic Acidemia Patients With CARBAGLU®: A Mixed Methods ApproachStatus: Recruiting, Estimated PCD: 2024-12-30
Clinical trial
Open-label, Single-arm, Multicenter Study to Assess the Safety of Cystadrops® in Pediatric Cystinosis Patients From 6 Months to Less Than 2 Years OldStatus: Completed, Estimated PCD: 2022-12-23
Clinical trial
A Non-Interventional Post-Authorization Safety Study (PASS) of Carbaglu® for the Treatment of Hyperammonemia Due to Methylmalonic Acidemia (MMA) and Propionic Acidemia (PA) in Adult and Pediatric Patient PopulationsStatus: Recruiting, Estimated PCD: 2032-06-30
Clinical trial
Efficacy, Safety and Pharmacokinetics of 3 Doses of REC 0/0559 Eye Drops for the Treatment of Stage 2 (Moderate) and 3 (Severe) Neurotrophic Keratitis in Adult PatientsStatus: Recruiting, Estimated PCD: 2024-04-01