Organization
Azafaros
1 clinical trial
Clinical trial
Randomized, Double Blind, Placebo Controlled, Multicenter, 12 Weeks Phase 2 Study to Evaluate the Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of Oral AZ-3102 in Patients With GM2 Gangliosidosis or Niemann-Pick Type C DiseaseStatus: Active (not recruiting), Estimated PCD: 2024-03-01