Organization
Leadiant Biosciences
2 clinical trials
Clinical trial
A Phase 3, Prospective, Randomized, Double-Blind, Placebo-Controlled, Multicenter Study of Chenodeoxycholic Acid (CDCA), With an Open-Label Cohort, in Newly Diagnosed Participants With Cerebrotendinous Xanthomatosis (CTX)Status: Not yet recruiting, Estimated PCD: 2025-11-30
Clinical trial
A Randomized, Double-Blind, Placebo-Controlled, Multi-Center Study to Evaluate the Efficacy of ManNAc in Subjects With GNE MyopathyStatus: Active (not recruiting), Estimated PCD: 2024-03-28