Organization
Terence Flotte
1 clinical trial
Clinical trial
A Two-Stage, Dose-Escalation and Safety & Efficacy Study of Bilateral Intraparenchymal Thalamic and Intracisternal/Intrathecal Administration of AXO-AAV-GM2 in Tay-Sachs or Sandhoff DiseaseStatus: Active (not recruiting), Estimated PCD: 2024-11-01