Organization
Taysha Gene Therapies
3 clinical trials
Clinical trial
Open-label, Randomized, Dose-escalation and Dose-expansion Study of the Safety and Preliminary Efficacy of a Single Intrathecal Administration of TSHA-102, an AAV9-Delivered Gene Therapy, in the Treatment of Adult Females With Rett SyndromeStatus: Recruiting, Estimated PCD: 2024-11-08
Clinical trial
A Multicenter, Open Label, Randomized, Dose-Escalation and Dose-Expansion Study of the Safety, Tolerability, and Efficacy of a Single Intrathecal Administration of TSHA-102, an AAV9-Delivered Gene Therapy, for the Treatment of Pediatric Females With Rett SyndromeStatus: Recruiting, Estimated PCD: 2028-11-02
Clinical trial
A Phase I Study of Intrathecal Administration of scAAV9/JeT-GAN for the Treatment of Giant Axonal NeuropathyStatus: Active (not recruiting), Estimated PCD: 2030-06-30