Product
ABO-102
Aliases
scAAV9.U1a.hSGSH, UX111
2 clinical trials
4 indications
Indication
Mucopolysaccharidosis type IIIAIndication
Sanfilippo syndromeIndication
Mucopolysaccharidosis type IIIIndication
MPS IIIClinical trial
Phase I/II/III Gene Transfer Clinical Trial of scAAV9.U1a.hSGSH for Mucopolysaccharidosis (MPS) IIIAStatus: Active (not recruiting), Estimated PCD: 2024-06-01
Clinical trial
A Phase I/II Open Label, Single-dose, Gene Transfer Study of scAAV9.U1a.hSGSH (ABO-102) in Patients With Middle and Advanced Phases of MPS IIIA DiseaseStatus: Terminated, Estimated PCD: 2022-03-10