Product
Sapropterin
Aliases
Kuvan
2 clinical trials
4 indications
Indication
PhenylketonuriaIndication
Behavior and Behavior MechanismsIndication
GTP Cyclohydrolase DeficiencyClinical trial
Evaluation of Behavior, Executive Function, Neurotransmitter Function and Genomic Expression in PKU "Nonresponders" to Kuvan® (Sapropterin Dihydrochloride)Status: Completed, Estimated PCD: 2013-12-01
Clinical trial
Pilot Study to Assess Impact of Kuvan® Supplementation as an Adjunct Treatment in Subjects With Dominantly-inherited GTPCH Deficiency on Mood, Behavioral and Motor PhenotypesStatus: Completed, Estimated PCD: 2013-08-01