Product
zilganersen
Aliases
ION373
1 clinical trial
1 indication
Indication
Alexander DiseaseClinical trial
A Phase 1-3, Double-Blind, Randomized, Placebo-Controlled Study to Evaluate the Efficacy, Safety, Pharmacokinetics and Pharmacodynamics of Intrathecally Administered Zilganersen (ION373) in Patients With Alexander DiseaseStatus: Recruiting, Estimated PCD: 2025-03-01