Product
Nula-Cel
Aliases
nula-cel Drug Product
1 clinical trial
1 indication
Indication
Sickle Cell DiseaseClinical trial
A Phase I/II Study of Nula-cel in Autologous CD34+ Hematopoietic Stem Cells to Convert HbS to HbA for Treating Severe Sickle Cell DiseaseStatus: Recruiting, Estimated PCD: 2026-07-31