Product
Auto CD34+PBSC transduced with a lentiviral vector encoding a novel coagulation factor VIII transgene
1 clinical trial
1 indication
Indication
Hemophilia AClinical trial
Gene Therapy for Hemophilia A With a High Expression Factor VIII Transgene in Autologous Hematopoietic Stem CellsStatus: Recruiting, Estimated PCD: 2025-01-01