Product
Nitisinone
Aliases
Orfadin®
Name
Orfadin
INN Name
Nitisinone
FDA Approved
Yes
1 clinical trial
5 organizations
2 indications
3 documents
Indication
Hereditary TyrosinemiaIndication
Type IClinical trial
A Prospective, Non-interventional, Post-Marketing Study to Describe Outcome of Nitisinone Treatment in Hereditary Tyrosinemia Type 1 (HT-1) Patients in Routine Clinical Care in ChinaStatus: Recruiting, Estimated PCD: 2027-06-30
Document
DailyMed Label: OrfadinOrganization
SWEDISH ORPHAN BIOVITRUM AB (PUBL)Document
DailyMed Label: NITYROrganization
Cycle Pharmaceuticals Ltd.Document
DailyMed Label: NitisinoneOrganization
Analog PharmaOrganization
Eton Pharmaceuticals, Inc.Organization
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