Product
ANB-004
Aliases
ANB-004, dose 1, ANB-004, dose 2, ANB-004, dose 3
1 clinical trial
1 indication
Indication
Spinal Muscular AtrophyClinical trial
An Open-Label, Non-Comparative Clinical Study of the Safety and Efficacy of an Adeno-Associated Viral Vector Carrying the SMN Gene (ANB-004 (JSC BIOCAD, Russia)) After a Single Intravenous Administration of Escalating Doses in Children With Spinal Muscular AtrophyStatus: Recruiting, Estimated PCD: 2025-09-01