Product
Tividenofusp alfa
Aliases
tividenofusp alfa
2 clinical trials
1 indication
Indication
MPS IIClinical trial
A Phase 1/2, Multicenter, Open-Label Study to Determine the Safety, Pharmacokinetics, and Pharmacodynamics of DNL310 in Pediatric Participants With Hunter SyndromeStatus: Active (not recruiting), Estimated PCD: 2027-07-01
Clinical trial
A Phase 2/3, Multicenter, Double-Blind, Randomized Study to Determine the Efficacy and Safety of DNL310 vs Idursulfase in Pediatric Participants With Neuronopathic or Non-Neuronopathic Mucopolysaccharidosis Type IIStatus: Recruiting, Estimated PCD: 2025-12-01