Product
rAAV5-miHTT
Aliases
AMT-130, intra-striatal rAAV5-miHTT
2 clinical trials
2 abstracts
1 indication
Indication
Huntington's diseaseClinical trial
A Phase I/II, Randomized, Double-Blind, Sham Control Study to Explore Safety, Tolerability, and Efficacy Signals of Multiple Doses of Striatally-Administered rAAV5-miHTT Total Huntingtin Gene (HTT) Lowering Therapy (AMT-130) in Early Manifest Huntington's DiseaseStatus: Recruiting, Estimated PCD: 2029-04-01
Clinical trial
A Phase Ib/II Randomized, Double-Blind Study to Explore Safety, Tolerability, and Efficacy Signals of Multiple Doses of Striatally-Administered rAAV5-miHTT Total Huntingtin Gene (HTT) Lowering Therapy (AMT 130) in Early Manifest Huntington's DiseaseStatus: Recruiting, Estimated PCD: 2029-03-01