Product
Cipaglucosidase alfa
2 clinical trials
2 indications
Indication
Pompe DiseaseClinical trial
A Global Prospective Observational Registry of Patients With Pompe DiseaseStatus: Recruiting, Estimated PCD: 2034-12-20
Clinical trial
An Open-label Study to Evaluate the Safety, Efficacy, Pharmacokinetics, Pharmacodynamics, and Immunogenicity of Cipaglucosidase Alfa/Miglustat in Both ERT-experienced and ERT-naïve Pediatric Subjects With Infantile-onset Pompe Disease Aged 0 to < 18 YearsStatus: Recruiting, Estimated PCD: 2027-04-01