Product
AAV2-hRPE65v2, voretigene neparvovec
1 clinical trial
2 indications
Indication
Leber Congenital AmaurosisIndication
Leber congenital amaurosisClinical trial
A Safety and Efficacy Study in Subjects With Leber Congenital Amaurosis (LCA) Using Adeno-Associated Viral Vector to Deliver the Gene for Human RPE65 to the Retinal Pigment Epithelium (RPE) [AAV2-hRPE65v2-301]Status: Active (not recruiting), Estimated PCD: 2015-07-01