Product
RNA antisense oligonucleotide
1 clinical trial
2 indications
Indication
Retinitis PigmentosaIndication
Usher syndrome type 2Clinical trial
An Open-Label Extension Study to Evaluate the Safety and Tolerability of QR 421a in Subjects With Retinitis Pigmentosa (RP) Due to Mutations in Exon 13 of the USH2A Gene (Helia)Status: Terminated, Estimated PCD: 2022-10-18