Product
EDIT-301
Aliases
reni-cel, renizgamglogene autogedtemcel
2 clinical trials
5 indications
Indication
Beta ThalassemiaIndication
HemoglobinopathiesIndication
Thalassemia MajorIndication
Beta-thalassemia intermediaIndication
Sickle Cell DiseaseClinical trial
A Multicenter Study to Evaluate the Safety, Tolerability, and Efficacy of a Single Dose of Autologous Clustered Regularly Interspaced Short Palindromic Repeats Gene-edited Cluster of Differentiation 34 (CD34+) Human Hematopoietic Stem and Progenitor Cells (HSPC) (EDIT-301) in Transfusion-Dependent Beta Thalassemia (TDT)Status: Recruiting, Estimated PCD: 2025-09-01
Clinical trial
A Phase 1/2 Study to Evaluate the Safety and Efficacy of a Single Dose of Autologous Clustered Regularly Interspaced Short Palindromic Repeats Gene-edited CD34+ Human Hematopoietic Stem and Progenitor Cells (EDIT-301) in Subjects With Severe Sickle Cell DiseaseStatus: Recruiting, Estimated PCD: 2025-08-01