Product

GNR-055

Aliases

GNR-055 1.0-2.0-3.0 mg/kg, GNR-055 2.0 mg/kg, GNR-055 3.0 mg/kg

1 clinical trial

2 indications

Indication

Mucopolysaccharidosis Type II

Indication

Metabolic Diseases

Clinical trial

Multicenter, Open-Label, Multi-cohort Study to Evaluate Safety, Pharmacokinetics, Pharmacodynamics, and Efficacy of Drug Product GNR 055 (JSC "GENERIUM", Russia) in Patients With Mucopolysaccharidosis Type II

Status: Recruiting, Estimated PCD: 2025-02-01