Indication
GNE Myopathy
2 clinical trials
2 products
Clinical trial
A Randomized, Double-Blind, Placebo-Controlled, Multi-Center Study to Evaluate the Efficacy of ManNAc in Subjects With GNE MyopathyStatus: Active (not recruiting), Estimated PCD: 2024-03-28
Product
ManNAcClinical trial
Phase 3B Open-Label Extension Study to Evaluate the Safety and Efficacy of Aceneuramic Acid Extended-Release (Ace-ER) Tablets in Patients With GNE Myopathy (GNEM) or Hereditary Inclusion Body Myopathy (HIBM)Status: Terminated, Estimated PCD: 2018-01-10
Product
Aceneuramic Acid