Product
Aceneuramic Acid
1 clinical trial
6 indications
Indication
Inclusion Body MyopathyIndication
Distal Myopathy With Rimmed VacuolesIndication
MyopathyIndication
Nemaline myopathyIndication
GNE MyopathyIndication
Quadriceps Sparing MyopathyClinical trial
Phase 3B Open-Label Extension Study to Evaluate the Safety and Efficacy of Aceneuramic Acid Extended-Release (Ace-ER) Tablets in Patients With GNE Myopathy (GNEM) or Hereditary Inclusion Body Myopathy (HIBM)Status: Terminated, Estimated PCD: 2018-01-10