Indication
Pelizaeus-Merzbacher Disease
3 clinical trials
3 products
Clinical trial
A Phase 1b Study to Evaluate the Safety, Pharmacokinetics and Pharmacodynamics of Intrathecally Administered ION356 in Patients With Pelizaeus Merzbacher DiseaseStatus: Recruiting, Estimated PCD: 2028-06-01
Product
ION356Clinical trial
Longitudinal Study of Neurodegenerative DisordersStatus: Recruiting, Estimated PCD: 2030-01-01
Clinical trial
Augmentation of Umbilical Cord Blood Transplantation for Inherited Metabolic Diseases With Intrathecal Administration of Human Umbilical Cord Blood-Derived Oligodendrocyte-Like CellsStatus: Recruiting, Estimated PCD: 2024-10-01
Product
DUOC-01