Product
ION356
1 clinical trial
1 indication
Indication
Pelizaeus-Merzbacher DiseaseClinical trial
A Phase 1b Study to Evaluate the Safety, Pharmacokinetics and Pharmacodynamics of Intrathecally Administered ION356 in Patients With Pelizaeus Merzbacher DiseaseStatus: Recruiting, Estimated PCD: 2028-06-01