Indication
Limb-girdle muscular dystrophy type 2I
2 clinical trials
2 products
Clinical trial
An Open Label Phase 2 Study of BBP-418 in Patients With Limb Girdle Muscular Dystrophy Type 2I (MLB-01-003)Status: Active (not recruiting), Estimated PCD: 2026-11-01
Product
BBP-418Clinical trial
A Two-part Multicenter Study: a Randomized, Double-blind, Placebo-controlled Dose-escalation Safety Phase (Part 1) Followed by Double-blind, Placebo-controlled, Adaptive Phase (Part 2) Study to Evaluate the Safety and Efficacy of AB-1003 in Adult Subjects With LGMD2I/R9 Mutations in the Gene Encoding Fukutin Related Protein (FKRP)Status: Recruiting, Estimated PCD: 2028-12-01
Product
AB-1003