Product
AB-1003
1 clinical trial
8 indications
Indication
Limb-Girdle Muscular DystrophyIndication
Limb-Girdle Muscular Dystrophy Type 2Indication
Limb-girdle muscular dystrophy type 2IIndication
Muscular DystrophyIndication
Limb-girdle muscular dystrophyIndication
FKRPIndication
FKRP MutationIndication
Fukutin Related ProteinClinical trial
A Two-part Multicenter Study: a Randomized, Double-blind, Placebo-controlled Dose-escalation Safety Phase (Part 1) Followed by Double-blind, Placebo-controlled, Adaptive Phase (Part 2) Study to Evaluate the Safety and Efficacy of AB-1003 in Adult Subjects With LGMD2I/R9 Mutations in the Gene Encoding Fukutin Related Protein (FKRP)Status: Recruiting, Estimated PCD: 2028-12-01