Indication
Hurler Syndrome
2 clinical trials
3 products
Clinical trial
A Multi-center, Randomized, Active Controlled Clinical Trial to Evaluate the Efficacy and Safety of OTL-203 in Subjects With Mucopolysaccharidosis Type I, Hurler Syndrome (MPS-IH) Compared to Standard of Care With Allogeneic Hematopoietic Stem Cell Transplantation (Allo-HSCT)Status: Recruiting, Estimated PCD: 2028-03-01
Product
OTL-203Product
Allo-HSCTClinical trial
Phase I/II Pilot Study of Mixed Chimerism to Treat Inherited Metabolic DisordersStatus: Terminated, Estimated PCD: 2016-04-01