Product
Hematopoietic Stem Cell Infusion
1 clinical trial
12 indications
Indication
Hurler SyndromeIndication
Mucopolysaccharidosis type IIndication
Hunter SyndromeIndication
Sanfilippo Syndrome (MPS III)Indication
Globoid LeukodystrophyIndication
Metachromatic LeukodystrophyIndication
AdrenoleukodystrophyIndication
Sandhoff diseaseIndication
Tay-Sachs diseaseIndication
Pelizaeus Merzbacher (PMD)Indication
Niemann-Pick DiseaseIndication
Alpha-mannosidosisClinical trial
Phase I/II Pilot Study of Mixed Chimerism to Treat Inherited Metabolic DisordersStatus: Terminated, Estimated PCD: 2016-04-01