Indication
Glycogen Storage Disease Type II (GSD II)
1 clinical trial
1 product
Product
GZ402666Clinical trial
An Open-label, Multicenter, Multinational, Ascending Dose Study of the Safety, Tolerability, Pharmacokinetics, Pharmacodynamics, and Exploratory Efficacy of Repeated Biweekly Infusions of neoGAA in naïve and Alglucosidase Alfa Treated Late-onset Pompe Disease Patients.Status: Completed, Estimated PCD: 2015-02-25