Product
GZ402666
1 clinical trial
3 indications
Indication
Pompe DiseaseIndication
Glycogen Storage Disease Type IIClinical trial
An Open-label, Multicenter, Multinational, Ascending Dose Study of the Safety, Tolerability, Pharmacokinetics, Pharmacodynamics, and Exploratory Efficacy of Repeated Biweekly Infusions of neoGAA in naïve and Alglucosidase Alfa Treated Late-onset Pompe Disease Patients.Status: Completed, Estimated PCD: 2015-02-25